ProQR Therapeutics N.V., a clinical-stage biotechnology company, focuses on the discovery and development of novel therapeutic medicines. The company develops an RNA editing platform through its Axiomer RNA editing technology for genetic disorders with unmet needs. Its lead product candidate, AX-0810, targets na-taurocholate cotransporting polypeptide (NTCP) for the treatment of cholestatic diseases. The company also develops AX-2402, which targets methyl CpG binding protein 2 mutations for Rett syndrome; AX-2911, which targets PNPLA3 for metabolic dysfunction-associated steatohepatitis; and AX-1412, which targets the B4GALT1 gene for cardiovascular diseases. It has a research and collaboration agreement with Eli Lilly and Company for the discovery, development, and commercialization of potential new medicines for genetic disorders in the liver and nervous system. The company was incorporated in 2012 and is headquartered in Leiden, the Netherlands.
Market Potential | Discover ProQR's target market in untreated cholestatic diseases, with analyst price targets ranging from $4 to $14 and a "Strong Buy" consensus |
Financial Health | Learn about ProQR's $141M cash reserve, funding operations until mid-2027, while managing higher-than-expected operating expenses |
Clinical Milestones | Delve into ProQR's lead candidate AX-0810 as it enters Phase 1 trials, with data expected in Q4 2025, potentially de-risking the entire platform |
RNA Editing Pionee | Explore ProQR Therapeutics' innovative Axiomer platform, poised to revolutionize treatments for genetic disorders, particularly cholestatic diseases |
Metrics to compare | PRQR | Sector Sector - Average of metrics from a broad group of related Healthcare sector companies | Relationship RelationshipPRQRPeersSector | |
|---|---|---|---|---|
P/E Ratio | −4.0x | −3.7x | −0.5x | |
PEG Ratio | 0.17 | −0.12 | 0.00 | |
Price / Book | 3.4x | 1.1x | 2.6x | |
Price / LTM Sales | 10.4x | 11.3x | 3.2x | |
Upside (Analyst Target) | 327.1% | 129.7% | 47.6% | |
Fair Value Upside | Unlock | −7.2% | 6.1% | Unlock |